TY - JOUR T1 - Developing standard procedures for pre-clinical efficacy studies in mouse models of spinal muscular atrophy JO - Neuromuscular Disorders PY - 2011/01/01 AU - Willmann R AU - Dubach J AU - Chen K ED - DO - DOI: 10.1016/j.nmd.2010.09.014 PB - Elsevier BV VL - 21 IS - 1 SP - 74 EP - 77 Y2 - 2024/09/19 ER -