TY - CONF T1 - Complete Rescue of SMA Mouse Model by Systemic Delivery of scAAV9 Mediating SMN Replacement JO - NEUROLOGY PY - 2010/03/02 AU - Valori C AU - Ning K AU - Wyles M AU - Azzouz M ED - VL - 74 IS - 9 SP - A287 EP - A287 Y2 - 2024/09/19 ER -