@misc{misc, title = {{Safety and efficacy of C9ORF72-repeat RNA nuclear export inhibition in amyotrophic lateral sclerosis}}, url = {{}}, year = {{2021}}, month = {{4}}, author = {{Castelli LM and Cutillo L and Souza CDS and Sanchez-Martinez A and Granata I and Myszczynska MA and Heath PR and Livesey MR and Ning K and Azzouz M and Shaw PJ et al}}, doi = {{10.1101/2021.04.12.438950}}, note = {{Accessed on 2024/09/19}}}