TY - CONF T1 - Current Advances in Gene Therapy for Spinal Muscular Atrophy JO - HUMAN GENE THERAPY PY - 2010/10/01 AU - Azzouz M AU - Valori C AU - Ning K AU - Wyles M ED - VL - 21 IS - 10 SP - 1388 EP - 1389 Y2 - 2024/09/19 ER -